September 2024 | Journal Articles

Human T cell generation is restored in CD3δ severe combined immunodeficiency through adenine base editing

Authors:DB, Kohn, GM, Crooks, DR, Liu, N., Wright, Z., Romero, L., Murguia-Favela, A., Narendran, CS, Seet, H., Gelfer, A., Azzun, KA, Everette, RL, Wong, V., Christian, J., Butler, A., Garibay, S-H L, Kang, X., Wu, ST, Fitz-Gibbon, B., Campo-Fernandez, GA, Newby, PC, Chang, G., Yiu, GE, McAuley

Published:Cell, 2023:186:7, 1398-1416