September 2024 | Journal Articles

Human T cell generation is restored in CD3δ severe combined immunodeficiency through adenine base editing

Authors: Romero, Christian, Kohn, Chang, Gelfer, Wu, Z., V., DB, PC, H., X., Wright, Wong, Newby, Seet, Kang, S-H L, N., RL, GA, CS, Garibay, Liu, McAuley, Everette, Campo-Fernandez, Narendran, A., DR, GE, KA, B., A., Butler, Crooks, Yiu, Azzun, Fitz-Gibbon, Murguia-Favela, J., GM, G., A., ST, L.

Published: Cell, 2023:186:7, 1398-1416

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